1020 Locust Street
Jefferson Alumni Hall, Suite 508
Philadelphia, PA 19107
(215) 503-1037
Jefferson Alumni Hall, Suite 508
Philadelphia, PA 19107
(215) 503-1037
Most Recent Peer-reviewed Publications
- Entorhinal cortical neurons are the primary targets of FUS mislocalization and ubiquitin aggregation in FUS transgenic rats
- Mutant TDP-43 in motor neurons promotes the onset and progression of ALS in rats
- Early exposure to paraquat sensitizes dopaminergic neurons to subsequent silencing of PINK1 gene expression in mice
- Temporal expression of mutant LRRK2 in adult rats impairs dopamine reuptake
- TDP-43 potentiates alpha-synuclein toxicity to dopaminergic neurons in transgenic mice
- FUS transgenic rats develop the phenotypes of amyotrophic lateral sclerosis and frontotemporal lobar degeneration
- Transgenic rat model of neurodegeneration caused by mutation in the TDP gene
- Nerve injection of viral vectors efficiently transfers transgenes into motor neurons and delivers RNAi therapy against ALS
- Developing tTA transgenic rats for inducible and reversible gene expression
- A tightly regulated Pol III promoter for synthesis of miRNA genes in tandem
- A construct with fluorescent indicators for conditional expression of miRNA
- Therapeutic gene silencing delivered by a chemically modified small interfering RNA against mutant SOD1 slows amyotrophic lateral sclerosis progression
- Allele-specific RNAi selectively silences mutant SOD1 and achieves significant therapeutic benefit in vivo
- Multiple shRNAs expressed by an inducible pol II promoter can knock down the expression of multiple target genes
- Transgenic RNAi: Accelerating and expanding reverse genetics in mammals
- Pol II-expressed shRNA knocks down Sod2 gene expression and causes phenotypes of the gene knockout in mice
- Pol II-expressed shRNA knocks down Sod2 gene expression and causes phenotypes of the gene knockout in mice.
- An RNA polymerase II construct synthesizes short-hairpin RNA with a quantitative indicator and mediates highly efficient RNAi
- Dominant disease gene gets silenced
- An RNA polymerase II construct synthesizes short-hairpin RNA with a quantitative indicator and mediates highly efficient RNAi.
