1020 Locust Street
Suite 393
Philadelphia, PA 19107
(215) 503-5715
Suite 393
Philadelphia, PA 19107
(215) 503-5715
Most Recent Peer-reviewed Publications
- Extended normal life after AAVrh10-mediated gene therapy in the mouse model of krabbe disease
- Effects of treatments on inflammatory and apoptotic markers in the CNS of mice with globoid cell leukodystrophy
- Insulin-like growth factor-1 provides protection against psychosine-induced apoptosis in cultured mouse oligodendrocyte progenitor cells using primarily the PI3K/Akt pathway
- Biochemical and pathological evaluation of long-lived mice with globoid cell leukodystrophy after bone marrow transplantation
- AAV-Mediated expression of galactocerebrosidase in brain results in attenuated symptoms and extended life span in murine models of globoid cell leukodystrophy